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Gene Therapy: A Transformative Shift in Rare Disease Treatment

After decades of promise, gene therapy is finally starting to deliver on its potential—especially for rare diseases. Diseases that were once death sentences are now manageable, if not curable, thanks to gene therapy breakthroughs.

In this expert video, Darren Bentley, PhD, Senior Director, Clinical Pharmacology explores how gene therapy is transforming rare disease treatment, while addressing a critical challenge: cost.

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